Hurler Syndrome - 26 Studies Found
Recruiting |
: BMT Abatacept for Non-Malignant Diseases :
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Recruiting |
: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis :
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Active, not recruiting |
: Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders :
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Recruiting |
: Mucopolysaccharidosis I (MPS I) Registry : Mucopolysaccharidosis I (MPS I) : 2005-09-02 |
RECRUITING |
: A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT : MPS-IH (Hurler Syndrome) : 2024-05-14 : Experimental: OTL-203: Autologous CD34+ enriched cell fraction that contains hematopoietic stem and progenitor cells transduced ex vivo using lentivir |